Gene Delivery and Gene Editing (GDE) Focus Group Scientific Session

Focus Group Scientific Session

Date/Time: Sunday, July 22, 2018 - 3:00 PM to 5:00 PM


This Gene Delivery and Editing (GDE) Focus Group session will focus on creating a better fundamental understanding of the barriers to gene delivery and editing, designing improved carriers, and realizing opportunities for therapeutic intervention. Relevant topics include nucleic acid-based approaches for generating therapeutic proteins (e.g. mRNA, pDNA), eliminating disease causing proteins (e.g. siRNA, miRNA, ASOs), and precisely editing the genome (e.g. CRISPR/Cas, TALENs, ZFNs). This session aims to learn from past successes in nucleic acid delivery, while also looking ahead to the challenges and opportunities in mRNA and CRISPR/Cas. The winners of the inaugural GDE Focus Group Young Investigator Award as well as the GDE Focus Group Student/PostDoc Award will also give their award lectures in this session.